Fighting Cholesterol Monsters in the Brain: A Promising Story of Cyclodextrin and Niemann-Pick C Disease

Introduction: A Battle of Tiny Titans Inside Our Cells Imaging a microscopic battleground inside your brain. You might not see it or even feel it immediately, but for some, this hidden war can have dire consequences. Niemann-Pick type C (NPC) disease is a rare but devastating neurodegenerative disorder that affects both young and old. Imagine […]

Decoding Sanfilippo Syndrome: A Journey Through the Murine Mind

— Introduction Imagine facing a world where your senses betray you, everyday tasks become insurmountable challenges, and life progresses at a rapid decline. This paints a picture similar to that experienced by children suffering from Sanfilippo Syndrome Type B, a rare genetic disorder encompassing a host of developmental shortfalls. But what if understanding this enigmatic […]